Research and Development

The Research and Development team at Expansion Therapeutics is responsible for pioneering the discovery and development of small molecule medicines targeting RNA-mediated diseases. This multidisciplinary team utilizes their expertise in computational chemistry, structural biology, and drug discovery to identify potent RNA binders and advance them from conceptual stages through preclinical development. They work collaboratively to generate novel RNA-targeted drug candidates, particularly focusing on treatments for expansion repeat diseases with currently limited therapeutic options.