Annemieke Aartsma-Rus

Annemieke is Professor of Translational Genetics at Leiden University as well as President of the Oligonucleotide Therapeutics Society (OTS) and chair of TREAT-NMD; a network for the neuromuscular field that provides an infrastructure to ensure that the most promising new therapies reach patients as quickly as possible. Annemieke is a world-leading expert in exon skipping therapies and played an important role in the development of the antisense mediated exon skipping therapy for Duchenne muscular dystrophy already during her Ph.D. research, and remains a scientific advisor for several Duchenne organizations. Her work to date has resulted in deep knowledge about potential pitfalls in oligonucleotide therapeutic drug discovery and development, and as President of OTS, Annemieke is well respected in the whole oligonucleotide therapeutics field.